Hydrostatic isolated limb perfusion with adeno-associated virus vectors enhances correction of skeletal muscle in Pompe disease (Q34332408)

1 August 2017

title

Hydrostatic isolated limb perfusion with adeno-associated virus vectors enhances correction of skeletal muscle in Pompe disease (English)

1 reference

1 August 2017

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A20686508

17 June 2024

author name string

B. Sun

1

1 reference

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17 June 2024

S. Li

2

1 reference

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17 June 2024

A. Bird

3

1 reference

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17 June 2024

D. D. Koeberl

4

1 reference

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17 June 2024

language of work or name

English

1 reference

National Center for Biotechnology Information

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/esummary.fcgi?db=pubmed&retmode=json&id=20686508

17 June 2024

publication date

5 August 2010

1 reference

full work available at URL

1 August 2017

https://europepmc.org/articles/pmc2988075?pdf=render

file format

Portable Document Format

online access status

open access

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https://www.ncbi.nlm.nih.gov/pmc/articles/pmid/20686508/pdf/?tool=EBI

17 June 2024

file format

Portable Document Format

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https://www.ncbi.nlm.nih.gov/pmc/articles/pmid/20686508/?tool=EBI

17 June 2024

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https://www.ebi.ac.uk/europepmc/webservices/rest/search?resulttype=core&format=json&query=SRC%3AMED%20AND%20EXT_ID%3A20686508

https://europepmc.org/articles/PMC2988075

17 June 2024

1 reference

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https://europepmc.org/articles/PMC2988075?pdf=render

17 June 2024

file format

Portable Document Format

online access status

open access

content deliverer

1 reference

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17 June 2024

1 reference

1 August 2017

volume

17

1 reference

1 August 2017

issue

12

1 reference

1 August 2017

page(s)

1500-1505

1 reference

Evaluation of hydrodynamic limb vein injections in nonhuman primates

1 August 2017

cites work

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Hydrodynamic limb vein injection of adeno-associated virus serotype 8 vector carrying canine myostatin propeptide gene into normal dogs enhances muscle growth

6 July 2018

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Enhanced efficacy of an AAV vector encoding chimeric, highly secreted acid alpha-glucosidase in glycogen storage disease type II.

6 July 2018

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6 July 2018

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6 July 2018

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Long-term intravenous treatment of Pompe disease with recombinant human alpha-glucosidase from milk

6 July 2018

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6 July 2018

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6 July 2018

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Recombinant human acid alpha-glucosidase enzyme therapy for infantile glycogen storage disease type II: results of a phase I/II clinical trial

6 July 2018

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Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

6 July 2018

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6 July 2018

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6 July 2018

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PubMed

https://pubmed.ncbi.nlm.nih.gov/20686508

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Magnetic resonance imaging-monitored plasmid DNA delivery in primate limb muscle

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/20686508

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/GT.2010.109

1 reference

1 August 2017

1 reference

1 August 2017

1 reference