Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells (Q24634829)

Stefan J Marciniak

13

0 references

Ignacio Varela

Ignacio Varela

4

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James P Di Santo

James P Di Santo

17

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Ludovic Vallier

Ludovic Vallier

20

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Helene Strick-Marchand

Helene Strick-Marchand

3

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David E Paschon

6

David E Paschon

0 references

Pei-Qi Liu

5

Pei-Qi Liu

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author name string

Kosuke Yusa

1

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S Tamir Rashid

2

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Adriana Ordóñez

8

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Nicholas R F Hannan

9

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Foad J Rouhani

10

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Sylvie Darche

11

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Graeme Alexander

12

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Noemi Fusaki

14

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Mamoru Hasegawa

15

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Michael C Holmes

16

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David A Lomas

18

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Allan Bradley

A conditional knockout resource for the genome-wide study of mouse gene function

19

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language of work or name

English

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publication date

20 October 2011

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published in

Nature

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volume

478

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issue

7369

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page(s)

391-4

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cites work

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Induction of pluripotent stem cells from adult human fibroblasts by defined factors

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Induced pluripotent stem cell lines derived from human somatic cells

7 April 2017

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Genome editing with engineered zinc finger nucleases

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Highly efficient endogenous human gene correction using designed zinc-finger nucleases

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7 April 2017

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Treatment of sickle cell anemia mouse model with iPS cells generated from autologous skin

7 April 2017

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A ROCK inhibitor permits survival of dissociated human embryonic stem cells

7 April 2017

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A highly efficient recombineering-based method for generating conditional knockout mutations

7 April 2017

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Efficient targeting of expressed and silent genes in human ESCs and iPSCs using zinc-finger nucleases

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A hyperactive piggyBac transposase for mammalian applications

7 April 2017

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Induced pluripotency: history, mechanisms, and applications

27 September 2017

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Modeling inherited metabolic disorders of the liver using human induced pluripotent stem cells.

27 September 2017

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A rapid and general assay for monitoring endogenous gene modification

27 September 2017

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Genome modification in human embryonic stem cells

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Gene targeting of a disease-related gene in human induced pluripotent stem and embryonic stem cells

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Human embryonic stem cells reveal recurrent genomic instability at 20q11.21.

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Recurrent chromosomal abnormalities in human embryonic stem cells

27 September 2017

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Autophagic disposal of the aggregation-prone protein that causes liver inflammation and carcinogenesis in alpha-1-antitrypsin deficiency

27 September 2017

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Generation of functional hepatocytes from human embryonic stem cells under chemically defined conditions that recapitulate liver development

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PubMed

https://pubmed.ncbi.nlm.nih.gov/21993621

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

An efficient and reversible transposable system for gene delivery and lineage-specific differentiation in human embryonic stem cells

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/21993621

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1038/NATURE10424

1 reference

Dimensions Publication ID

1038728338

0 references

1 reference

1 reference

PubMed publication ID

21993621

1 reference