September 18, 2024

PPMD & Global Patient Advocacy Groups Award BIND Project $113,000 to Further Brain Involvement Research

PPMD is thrilled to announce that we have collaborated with a number of patient organizations around the globe to provide Leiden University Medical Center (LUMC), together with the Duchenne Data Foundation (DDF), funding to further…

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September 17, 2024

Navigating Access & Resources

Navigating Access & Resources Navigating insurance access for medical care such as approved therapies or equipment can be daunting. Parents, patients, and healthcare providers spend hours putting together documents and speaking on the phone trying…

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September 12, 2024

Watch the Recording: Advocating for A Successful School Year

Recently, PPMD’s Alexis Hazlett was joined by panelists Jodi Krause (Colorado Children’s Hospital), Jill Castle, and Patrick Moeschen to discuss advocating for your child throughout the school year. The speakers dove into the differences between…

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September 9, 2024

Setting Up A Successful School Year

Setting Up A Successful School Year PPMD is here to make sure that families within the Duchenne and Becker community have the necessary tools to advocate for their child not only in medical settings, but…

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September 6, 2024

Raising Our Voices for Duchenne: Recap of PPMD’s Advocacy Webinar

On Thursday, September 5, 2024, PPMD hosted a special webinar, “PPMD Advocacy: Raising Our Voices in 2024 and Beyond,” bringing together advocates to reflect on PPMD’s advocacy efforts in our 30th anniversary year and discuss…

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September 5, 2024

Myology Course Educates and Advances Next Generation of Neuromuscular Physicians and Scientists

PPMD is dedicated to fighting for every future as we strive to end Duchenne. Since 2011, PPMD has been a proud supporter of the Myology Course, presented by Nationwide Children’s Hospital (NCH) and The Ohio…

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September 4, 2024

Introducing PPMD’s Newborn Screening Action Center: A Hub for Advocacy and Education

We are thrilled to announce the launch of PPMD’s Newborn Screening Action Center, a powerful resource designed to both educate and empower you as we work to ensure that every baby, in every state, has…

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September 3, 2024

Dyne Therapeutics Announces Positive New Clinical Data from Phase 1/2 DELIVER Trial of DYNE-251 in Duchenne

Dyne Therapeutics, Inc. has announced positive new clinical data from its ongoing Phase 1/2 DELIVER trial of DYNE-251 in patients with Duchenne who are amenable to exon 51 skipping. DYNE-251 is an exon skipping product…

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September 1, 2024

Raising Our Voices This Duchenne Action Month

PPMD is excited to join forces with fellow Duchenne-specific organizations from around the world to celebrate World Duchenne Awareness Day on September 7! This global initiative, spearheaded by the World Duchenne Organization, aims to raise…

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August 23, 2024

Duchenne Added to Massachusetts Newborn Screening Panel

PPMD is excited to announce another significant milestone: Massachusetts has officially approved the addition of Duchenne to the state’s newborn screening panel! The addition of Duchenne to the Commonwealth’s newborn screen panel was included as…

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