Vitamin B3 modulates mitochondrial vulnerability and prevents glaucoma in aged mice

Science. 2017 Feb 17;355(6326):756-760. doi: 10.1126/science.aal0092.

Abstract

Glaucomas are neurodegenerative diseases that cause vision loss, especially in the elderly. The mechanisms initiating glaucoma and driving neuronal vulnerability during normal aging are unknown. Studying glaucoma-prone mice, we show that mitochondrial abnormalities are an early driver of neuronal dysfunction, occurring before detectable degeneration. Retinal levels of nicotinamide adenine dinucleotide (NAD+, a key molecule in energy and redox metabolism) decrease with age and render aging neurons vulnerable to disease-related insults. Oral administration of the NAD+ precursor nicotinamide (vitamin B3), and/or gene therapy (driving expression of Nmnat1, a key NAD+-producing enzyme), was protective both prophylactically and as an intervention. At the highest dose tested, 93% of eyes did not develop glaucoma. This supports therapeutic use of vitamin B3 in glaucoma and potentially other age-related neurodegenerations.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aging / metabolism*
  • Aging / pathology
  • Animals
  • Cellular Senescence
  • Genetic Therapy
  • Glaucoma / pathology
  • Glaucoma / prevention & control*
  • Mice
  • Mitochondria / drug effects*
  • Mitochondria / pathology
  • NAD / deficiency*
  • Neurodegenerative Diseases / pathology
  • Neurodegenerative Diseases / prevention & control*
  • Neurons / metabolism
  • Neurons / pathology
  • Niacinamide / administration & dosage*
  • Niacinamide / metabolism
  • Niacinamide / pharmacology
  • Nicotinamide-Nucleotide Adenylyltransferase / genetics
  • Retinal Ganglion Cells / drug effects
  • Retinal Ganglion Cells / metabolism
  • Retinal Ganglion Cells / pathology

Substances

  • NAD
  • Niacinamide
  • Nicotinamide-Nucleotide Adenylyltransferase
  • Nmnat1 protein, mouse