Cross talk of combined gene and cell therapy in ischemic heart disease: role of exosomal microRNA transfer

Circulation. 2014 Sep 9;130(11 Suppl 1):S60-9. doi: 10.1161/CIRCULATIONAHA.113.007917.

Abstract

Background: Despite the promise shown by stem cells for restoration of cardiac function after myocardial infarction, the poor survival of transplanted cells has been a major issue. Hypoxia-inducible factor-1 (HIF1) is a transcription factor that mediates adaptive responses to ischemia. Here, we hypothesize that codelivery of cardiac progenitor cells (CPCs) with a nonviral minicircle plasmid carrying HIF1 (MC-HIF1) into the ischemic myocardium can improve the survival of transplanted CPCs.

Methods and results: After myocardial infarction, CPCs were codelivered intramyocardially into adult NOD/SCID mice with saline, MC-green fluorescent protein, or MC-HIF1 versus MC-HIF1 alone (n=10 per group). Bioluminescence imaging demonstrated better survival when CPCs were codelivered with MC-HIF1. Importantly, echocardiography showed mice injected with CPCs+MC-HIF1 had the highest ejection fraction 6 weeks after myocardial infarction (57.1±2.6%; P=0.002) followed by MC-HIF1 alone (48.5±2.6%; P=0.04), with no significant protection for CPCs+MC-green fluorescent protein (44.8±3.3%; P=NS) when compared with saline control (38.7±3.2%). In vitro mechanistic studies confirmed that cardiac endothelial cells produced exosomes that were actively internalized by recipient CPCs. Exosomes purified from endothelial cells overexpressing HIF1 had higher contents of miR-126 and miR-210. These microRNAs activated prosurvival kinases and induced a glycolytic switch in recipient CPCs, giving them increased tolerance when subjected to in vitro hypoxic stress. Inhibiting both of these miRs blocked the protective effects of the exosomes.

Conclusions: In summary, HIF1 can be used to modulate the host microenvironment for improving survival of transplanted cells. The exosomal transfer of miRs from host cells to transplanted cells represents a unique mechanism that can be potentially targeted for improving survival of transplanted cells.

Keywords: exosomes; genetic therapy; hypoxia-inducible factor-1; microRNAs; stem cells.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult Stem Cells / transplantation*
  • Animals
  • Cell Communication
  • Cellular Microenvironment
  • Combined Modality Therapy
  • Culture Media, Conditioned
  • DNA, Circular
  • Exosomes*
  • Female
  • Genetic Therapy*
  • Genetic Vectors / therapeutic use
  • Graft Survival
  • Hypoxia-Inducible Factor 1, alpha Subunit / genetics
  • Hypoxia-Inducible Factor 1, alpha Subunit / therapeutic use*
  • Male
  • Mice
  • Mice, Inbred NOD
  • Mice, SCID
  • Mice, Transgenic
  • MicroRNAs / genetics
  • MicroRNAs / therapeutic use*
  • Multipotent Stem Cells / transplantation*
  • Myocardial Infarction / genetics
  • Myocardial Infarction / surgery
  • Myocardial Infarction / therapy*
  • Myocardial Ischemia / genetics
  • Myocardial Ischemia / surgery
  • Myocardial Ischemia / therapy*
  • Neovascularization, Physiologic
  • Plasmids
  • Random Allocation
  • Transfection

Substances

  • Culture Media, Conditioned
  • DNA, Circular
  • Hypoxia-Inducible Factor 1, alpha Subunit
  • MIRN126 microRNA, mouse
  • MIRN210 microRNA, mouse
  • MicroRNAs